"This study is a breakthrough for our research group after years of work. When we reduce the production of the enzyme in mice, the development of all the clinical symptoms of progeria is reduced or blocked. We have also studied cultured cells from children with progeria, and can see that when the

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RuiYi Inc. announced that it has entered into an exclusive license and collaborative development agreement with Genor BioPharma for the development of RYI-008 in China. RYI-008 is a novel anti-IL-6 monoclonal antibody with a unique pharmacologic profile that has the potential to define a new "RYI-

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MultiCell Technologies, Inc. is pleased to announce the filing of a U.S. patent application concerning methods and formulations to achieve targeted tumor cell death. MCT-485 is a noncoding double stranded micro RNA (miRNA) which has demonstrated oncolytic and immune stimulating activity in in vitro

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Ultragenyx Pharmaceutical Inc., a biotechnology company focused on developing treatments for rare and ultra-rare genetic disorders, announced a Phase 1/2 study of UX003 for mucopolysaccharidosis type 7 (MPS 7, or Sly Syndrome). UX003 is a recombinant human b-glucuronidase intended as an enzyme The

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Raising hopes for cell-based therapies, UC San Francisco researchers have created the first functioning human thymus tissue from embryonic stem cells in the laboratory. The researchers showed that, in mice, the tissue can be used to foster the development of white blood cells the body needs to The

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“There is nothing like a mom or dad on a missionThat’s Shelby Swann’s simple explanation for all she does for her 8-year-old daughter Kendall, the International Rett Syndrome Foundation and other parents whose children also are afflicted with this genetic neurological disorderThe IRSF Strol

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THE successful battle to approve life-changing cystic fibrosis treatment should be a herald a new dawn for pharmaceutical drugs in Wales, an Assembly Member has saidLast week Health Minister Mark Drakeford went against his advisors and allowed Kalydeco to be made available on the Welsh NHSPlaid C

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Northwestern University scientists have shown a gene involved in neurodegenerative disease also plays a critical role in the proper function of the circadian clockIn a study of the common fruit fly, the researchers found the gene, called Ataxin-2, keeps the clock responsible for sleeping and wakin

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A study led by researchers from Plymouth University Peninsula Schools of Medicine and Dentistry has for the first time revealed how the loss of a particular tumour suppressing protein leads to the abnormal growth of tumours of the brain and nervous systemThe study is published in Brain: A Journal

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Imaging scans following treatment for diffuse large B-cell lymphoma do little to help detect a relapse, a Mayo Clinic study has found. The overwhelming majority of patients with this aggressive lymphoma already have symptoms, an abnormal physical exam or an abnormal blood test at the time of "Our

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